A gene therapy that patients breathe in has been found to shrink lung tumours by inserting immune-boosting genes into ...

Adeno-associated virus (AAV) has emerged as a reliable vehicle for delivering therapeutic DNA into patient cells, with eight AAV-based gene therapies approved worldwide as of mid-2025. 1 Yet questions ...

All participants had adverse events, but most were moderate in severity ...

According to data published by Precedence Research, the gene therapy industry is experiencing significant growth, transitioning from small-scale, high-cost production to large-scale, cost-effective ...

In cancer therapy research, scientists harness viruses and gene transfer to trigger immune-driven tumor destruction, offering hope against hard-to-treat melanoma. Study: A virus based vaccine combined ...

Delivery of therapeutic genes is essential for gene therapy. Adeno-associated viruses (AAVs) are a prime vector for carrying ...

In preclinical work recently published in Nature Communications, Fred Hutch Cancer Center scientists used a genetic “chain reaction” to transform herpes simplex virus DNA during an HSV infection. The ...

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the amount of blood the heart can pump and dramatically improves ...

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...

lt;pgt;Scientists have successfully reconstructed a virus thousands of years after it became extinct, a development they believe could herald a new step in treating genetic diseases such as cystic ...

For many patients, participating in gene therapy clinical trials isn't an option because their immune system recognizes and fights the helpful virus used for treatment. Now, University of Florida ...